Scott Gottlieb Expects the FDA to Approve 40 Gene Therapies by 2022
FDA commissioner, Scott Gottlieb said that he expects the FDA to approve 40 gene therapies by 2022 in a fireside chat at the 2018 BIO International Convention.
Gene Therapy
Singapore Could be the Second Country to Legalise Three Parent IVF, and With a New Method Too
Singapore could become the second country to legalise MRT but they are considering a new method that differs from the two currently legal in the UK.
Axovant Pivoting Towards Gene Therapies
Axovant has licensed Oxford Biomedica’s gene therapy for Parkinson’s disease, OXB-102 and brought in Dr Fraser Wright to act as their new Chief Technology Officer.
Tailored Vaccine Boosts Survival for Some Brain Cancer Patients
In a new multicenter clinical trial, a personalised vaccine improved the survival rates of some people with the deadly brain cancer glioblastoma.
Biotech Companies Race to Bring Gene Therapies to Market, While States Are Too Slow To Adopt
Whilst biotech companies are rushing to bring transformative gene therapies to market, states are too slow on adopting screening tests for genetic diseases that are, increasingly, treatable.
Disney Magic Creates Alternative To CRISPR
Interested in novel science and its applications, but sick to death of hearing about CRISPR? Then this story is for you.
Scientists Are ‘Training’ Virus to Attack Ovarian Cancer Cells
Although reprogrammed viruses are commonly used in gene therapy to treat diseases, this virus can do its work without affecting healthy cells.
Implanting Stem Cell ‘Patch’ Can Restore Vision
Researchers have developed a specially engineered retinal patch to treat people with sudden, severe sight loss.
Genetics Pioneer, George Church Wants to Reverse Ageing Using Gene Therapy
George Church’s idea is to “have the body and mind of a 22-year-old but the experience of a 130-year-old,” and himself might be one of the first volunteers to try the approach in humans.
Scientists Have Found the ‘Master Activator’ Gene for Cancer Spread
After 10 years of research, a team of Taiwanese scientists have identified a gene that plays a major role in triggering metastasis of cancer cells.
The Big Data Revolution is About to Change How We See the NHS Forever
Much of medicine is about information — the data that helps doctors make the right choices about our treatment. So how will the revolution in big data impact complex healthcare systems like the NHS?
Real-Time Activation of Target Genes in Specific Locations in the Genome
Researchers have created tools that would enable real-time activation of target genes in specific locations in the genome.
Treating Haemophilia B for Life, With One Single Injection
Now, Salk researchers have demonstrated in mice that haemophilia B can be treated for life with one single injection, containing disease-free liver cells that can produce their missing clotting factor.
Immunotherapy: Training the Body to Fight Cancer
Armed with new insights into the interactions between cancer and the immune system, research teams are developing novel treatments to harness the full potential of the body’s natural defenses.
New Method Can Predict How a Patient Will Respond to Chemotherapy Before Treatment
Less than half the patients diagnosed with cancer respond favourably to chemotherapy. Now, a new method for testing how patients will respond to various drugs could pave the way for more personalised treatment.
