FDA commissioner, Scott Gottlieb said that he expects the FDA to approve 40 gene therapies by 2022 in a fireside chat at the 2018 BIO International Convention.
Singapore could become the second country to legalise MRT but they are considering a new method that differs from the two currently legal in the UK.
In a new multicenter clinical trial, a personalised vaccine improved the survival rates of some people with the deadly brain cancer glioblastoma.
Whilst biotech companies are rushing to bring transformative gene therapies to market, states are too slow on adopting screening tests for genetic diseases that are, increasingly, treatable.
Although reprogrammed viruses are commonly used in gene therapy to treat diseases, this virus can do its work without affecting healthy cells.
George Church’s idea is to “have the body and mind of a 22-year-old but the experience of a 130-year-old,” and himself might be one of the first volunteers to try the approach in humans.
After 10 years of research, a team of Taiwanese scientists have identified a gene that plays a major role in triggering metastasis of cancer cells.
Much of medicine is about information — the data that helps doctors make the right choices about our treatment. So how will the revolution in big data impact complex healthcare systems like the NHS?
Researchers have created tools that would enable real-time activation of target genes in specific locations in the genome.
Now, Salk researchers have demonstrated in mice that haemophilia B can be treated for life with one single injection, containing disease-free liver cells that can produce their missing clotting factor.
Less than half the patients diagnosed with cancer respond favourably to chemotherapy. Now, a new method for testing how patients will respond to various drugs could pave the way for more personalised treatment.