Improvements to gene-editing techniques hold promise for inactivating the defective gene responsible for Huntington’s Disease.
Altering the genome, typically to better understand gene and protein function. This also paves the way for gene therapy.
U.S. drugmaker Gilead Sciences has announced that it will use Sangamo Therapeutics gene-editing technology to develop cancer treatments in a deal worth potentially $3 billion to Sangamo.
Last year, a scientific journal challenged just how “revolutionary” CRISPR was, claiming that it caused unintended gene mutations. But, a recent study proves how this was simply all just an over exaggeration.
DNA twitches during transcription to bring distant regions in contact and enhance gene expression, according to Stanford researchers, who devised a new way to label individual, nonrepetitive DNA sequences.
Scientists have tweaked the DNA in human heart cells to correct mutations that cause a deadly disease, which if proved safe could eventually cure children of Duchenne Muscular Dystrophy (DMD).
A new animal study involving virally-delivered gene therapies has indicated that high treatment doses might not be as safe as previous human trials have suggested